Duchenne Muscular Dystrophy (DMD) Industry Symposium – 11 July 2025, Prague TREAT-NMD™ is hosting a one-day, expert-led symposium on Duchenne Muscular Dystrophy (DMD) in Prague, Czech Republic, tailored for industry professionals looking to gain a comprehensive understanding of this complex field. Topics include: ✅ Clinical aspects & disease management ✅ Genetic causes & pathophysiology ✅ Preclinical models & therapeutic landscape ✅ Clinical trial design & outcome measures This symposium offers a practical, collaborative platform to explore key developments and challenges in DMD therapy. 🔹 Limited places available – register your interest now: #DMD #NeuromuscularResearch #Duchenne #ClinicalTrials #Pharma #Biotech #TREATNMD #NeuromuscularDiseases #LifeSciences #Prague2025

Reflecting on EVELAM 2024: Advancing Myology in Latin America Last November, over 240 professionals gathered in Urubamba, Peru, for the 17th Euro-Latin-American Summer School of Myology (EVELAM 2024). Experts from across Europe and Latin America came together to share insights on neuromuscular diseases, genetic testing, physiotherapy, and treatment strategies. With engaging workshops, in-depth discussions, and a strong collaborative spirit, the event showcased the latest developments in the field. EVELAM 2025 will take place in San José, Costa Rica, in December—stay tuned for more details. 🔗 Read the full event highlights: #EVELAM2024 #NeuromuscularDiseases #Myology #MedicalEducation #Collaboration #TREATNMD #WorldMuscleSociety

Join TREAT-NMD™ as a proud partner of the 2025 @MDAorg Clinical & Scientific Conference in Dallas, March 16-19. The conference will explore the latest research advancements and clinical achievements in #neuromuscular disease. TREAT-NMD™ is contributing in partnership with MDA to deliver a focused discussion on Pompe Disease: Mechanisms, Therapeutic Advances, Advocacy, and Integrated Care Approaches, chaired by Dr Priya Kishnani. 📅 Tuesday, 18th March at 8:30 – 10:30 AM On Monday 17th at 2pm we'll also be giving key talks on: 🔹 Project PaLaDIn @eu_paladin : David Allison, TREAT-NMD™ CEO, will present insights into this innovative programme advancing neuromuscular care. 🔹 TACT: Lindsay Alfano will highlight the vital role of the TREAT-NMD™ Advisory Committee for Therapeutics in providing expert guidance to therapeutic developers. We hope to see you at this fantastic conference! 🔗 Find out more and save the date > #MDAconference #MDA #Neuromuscular #MuscularDystrophy #ALS

Mark your calendar: Key Upcoming Events in the Neuromuscular Disease Field From expert-led masterclasses to collaborative symposiums, 2025 is packed with valuable opportunities for healthcare professionals, researchers, and industry leaders in the neuromuscular disease field. Stay informed, plan ahead, and make the most of these events by checking out our curated list of key dates. 🔗 Explore upcoming events here: #NeuromuscularResearch #ClinicalEducation #MedicalConferences #Neurology #TREATNMD

Today we hosted our first Expert Myotonic Dystrophy Type 1 Masterclass! It was a fantastic educational day where delegates joined virtually from all over the world to hear from experts in the field. Thanks to all our wonderful speakers and especially Nicholas Johnson and Benedikt Schoser who chaired the event. Also thank you to our sponsors @Dyne_tx , Lupin Neurosciences and @myTomorrows , without their support the event would not have been possible! If you missed it or want to stay updated on future events, follow us or visit our website for more information. #virtualevent #DM1 #experts #musculardystrophy #healthcareprofessionals

At the @MDAorg Clinical & Scientific Conference 2025, learn how the TREAT-NMD® Advisory Committee for Therapeutics (TACT) provides strategic guidance to bring therapies for neuromuscular diseases to life. Lindsay Alfano will share insights on TACT’s role in advancing drug development with multidisciplinary expertise and tailored advice as part of the "Innovative Research Programs: Filling Gaps in Therapeutic Development" session: 📅 March 17, 2025 ��� 2:00 – 3:30 AM 📍Hilton Anatole, Dallas, TX Be part of the conversation driving meaningful change for neuromuscular care. Learn more: #TACTGuidance #TherapeuticDevelopment #MDAconference #Research

Register Your Interest: SMA/DMD Educational Masterclasses in Prague! Join TREAT-NMD® for expert-led masterclasses tailored for European healthcare professionals involved in diagnosing and managing Duchenne muscular dystrophy (DMD) and Spinal muscular atrophy (SMA). 📍 Prague, Czech Republic 📅 8th – 10th July 2025 The Spinal Muscular Atrophy Masterclass, chaired by Prof. Laurent Servais , runs on 8th and 9th (morning) July, while the Duchenne Muscular Dystrophy Masterclass, chaired by Prof. Annemieke Aartsma-Rus -@oligogirl, runs on 9th (afternoon) and 10th July. This free-to-attend event includes a generous travel contribution, providing healthcare professionals with a unique opportunity to learn from leading experts and connect with peers across Europe. Register your interest now at Don’t miss this unique opportunity to enhance your expertise and contribute to advancing care for SMA and DMD patients. 🌍 #SMA #DMD #TREATNMD #HealthcareProfessionals

Join Us in Montreal for our upcoming Limb-Girdle Muscular Dystrophy Masterclass! Are you involved in diagnosing or managing Limb-Girdle muscular dystrophy (LGMD)? This April 2025, join TREAT-NMD™ in Montreal, Canada, for an in-person educational event designed for healthcare professionals in the neuromuscular field. Why Attend? ✅ Free to Attend ✅ Travel & Accommodation Support Provided ✅ Learn from Leading Experts ✅ Interactive, Hands-On Sessions This masterclass is ideal for professionals seeking to deepen their understanding of LGMD care and management while engaging with peers and industry leaders. Spaces are limited, so register your interest today 👉 For more details, contact us at education@treat-nmd.com. Let’s advance expertise and improve outcomes for patients together! #LimbGirdleMuscularDystrophy #LGMD #NeuromuscularDiseases #RareDiseases #MedicalEducation #NeuromuscularMedicine #Healthcare

Join TREAT-NMD® at the @MDAorg Clinical & Scientific Conference 2025 as our CEO David Allison discusses @eu_paladin , an innovative initiative shaping care pathways for neuromuscular diseases. Explore the future of therapeutic development during his talk, happening at the conference. 📅 March 17, 2025 ⏰ 2:00 – 3:30 AM 📍Hilton Anatole, Dallas, TX Be part of the conversation driving meaningful change for neuromuscular care. Learn more: ttps://www.mdaconference.org/ #ProjectPaLaDIn #MDAconference #MuscularDystrophy

TREAT-NMD is thrilled to announce an in-person, expert-led one-day symposium on Duchenne Muscular Dystrophy (DMD) in Prague, Czech Republic, on July 11th, 2025! This event is perfect for industry professionals new to the field of Duchenne and those seeking a comprehensive overview of this complex area. 💡 Topics Covered ✅ Clinical aspects of the disease ✅ Disease management ✅ Genetic causes and pathophysiology ✅ Preclinical tools and models ✅ DMD therapeutic landscape ✅ Clinical trial design ✅ Outcome measures for therapy development 🎯 Objectives 🔹 Equip participants with practical insights to apply in their work 🔹 Create a collaborative platform for sharing ideas, addressing challenges, and celebrating successes 📢 Limited Places Available! Be the first to know when registration opens—complete the expression of interest form now! 👇 #Duchenne #TREATNMD #NeuromuscularDiseases #DMD #LifeSciences #Prague2025

Explore the latest in Pompe disease research at the @MDAorg Muscular Dystrophy Association Clinical & Scientific Conference 2025! We are partnering with MDA to host, Pompe Disease: Mechanisms, Therapeutic Advances, Advocacy, and Integrated Care Approaches. This collaborative session, chaired by Dr Priya Kishnani, brings together global expertise to tackle key challenges in understanding and treating Pompe disease. 📅 March 18, 2025 ⏰ 8:30 – 10:30 AM 📍Hilton Anatole, Dallas, TX Don’t miss it! Learn more: #PompeDisease #MDAconference #MDA #Neuromuscular #MuscularDystrophy

As 2024 comes to an end, we would like to extend our heartfelt thank you to everyone that has supported the mission of TREAT-NMD®. Whether you have been actively involved in a project, contributed to funding, participated in a masterclass or shared a social media post, together we have played a crucial role in accelerating the development of effective treatments and establishing the best in diagnosis and care for people living with neuromuscular diseases worldwide. You can read about some of the progress we've made in our end of year Newsletter > While there is still much work to do, we look forward to being stronger together in 2025! #TREATNMD #EndOfYearReflection #NeuromuscularDiseases #ProgressThroughCollaboration

Join TREAT-NMD as a proud partner of the @MDAorg Muscular Dystrophy Association Clinical & Scientific Conference in Dallas, March 16-19. The conference will explore the latest research advancements and clinical achievements in #neuromuscular disease. TREAT-NMD is contributing in partnership with MDA to deliver a focused discussion on Pompe Disease: Mechanisms, Therapeutic Advances, Advocacy, and Integrated Care Approaches, chaired by Dr Priya Kishnani. 📅 Tuesday, 18th March at 8:30 – 10:30 AM On Monday 17th at 2pm we'll also be giving key talks on: 🔹 Project PaLaDIn: David Allison, TREAT-NMD CEO, will present insights into this innovative programme advancing neuromuscular care. 🔹 TACT: Lindsay Alfano will highlight the vital role of the TREAT-NMD Advisory Committee for Therapeutics in providing expert guidance to therapeutic developers. We hope to see you at this fantastic conference! 🔗 Find out more and save the date > #MDAconference #MDA #Neuromuscular #MuscularDystrophy #ALS

Join the TREAT-NMD Team as a Project Manager We’re looking for a skilled and motivated Project Manager to lead TREAT-NMD’s European IHI-funded project PaLaDIn @eu_paladin . This hybrid role is based in Newcastle upon Tyne and offers the opportunity to work with international stakeholders on an impactful initiative. If you have a strong background in project management, experience with Innovate UK or European Commission-funded projects, and excellent organisational skills, we’d love to hear from you. 📅 Application deadline: 5 January 2025 📍 Expected start date: 20 January 2025 Find out more and apply here: #ProjectManager #JobOpportunity #HybridWork

Welcome to the Team, Matt Freer! We’re delighted to introduce Matt Freer, TREAT-NMD’s new Business Development and Fundraising Manager. Matt is an experienced professional with a strong background in biotech, life sciences, and biological research. At TREAT-NMD, Matt will work across key areas such as patient education, global patient registries, and industry partnerships, helping to advance research and development in neuromuscular disorders. He also serves on the Scientific Advisory Board for FRAME, advocating for ethical alternatives to animal testing and championing non-animal research methods. Matt will be personally reaching out to introduce himself to all our partners soon. In the meantime, if you’d like to discuss anything or arrange a meeting, please get in touch here: #NewHire #TeamTREATNMD #BusinessDevelopment #NeuromuscularResearch

Limb Girdle muscular dystrophy (LGMD) Masterclass 🗓 April 2025 📍 Montreal, Canada Join TREAT-NMD for an in-person educational masterclass designed for North American healthcare professionals involved in diagnosing and managing the care of patients with LGMD and those working in the neuromuscular field that wish to enhance their expertise in this area. Event Highlights: ✅ Free to attend ✅ TREAT-NMD will contribute towards travel and accommodation costs ✅ Interactive sessions with leading experts Spaces are limited so please register you interest in attending here >  For more information about this event please contact us on education@treat-nmd.com #LimbGirdleMuscularDystrophy #LGMD #NeuromusularDiseases #RareDiseases #NMDS #MedicalEducation #NeuromuscularMedicine

Duchenne Muscular Dystrophy Therapeutic Pipeline Update We have recently completed our annual update to the Duchenne Muscular Dystrophy (DMD) therapeutic pipeline overview. This valuable resource provides patients and parents with detailed information on the various therapeutic approaches currently being investigated in clinical trials or approved for DMD. The overview highlights the advantages and disadvantages of each approach, as well as the hurdles that must be overcome before these therapies can be widely applied to patients. Our thanks go to Professor Annemieke Aartsma-Rus @oligogirl for her dedicated work in updating this on behalf of TREAT-NMD. To access the updated DMD therapeutic pipeline overview, visit our website> #Duchenne #DMDResearch #PatientCare #NeuromuscularDisorders #RareDiseaseTherapies

📣 Registration of Interest Open: TREAT-NMD Expert Masterclasses for SMA and DMD Please register* to attend our Expert masterclasses to be held in PRAGUE, Czech Republic - 1.5 day masterclass for diagnosing and managing Spinal muscular atrophy on 8th and 9th July 2025 - 1.5 day masterclass for diagnosing and managing Duchenne muscular dystrophy on 9th and 10th July 2025 This event is designed for healthcare professionals involved in diagnosing and managing DMD and/or SMA. Gain the latest insights on diagnostic pathways, standards of care, and emerging therapies, while engaging with experts, and peers to enhance DMD and SMA care. This is a free event with a generous contribution for travel and expenses. *Places are limited, and registration does not guarantee a place. Please do not book travel or accommodation until you have been offered a place to attend. Register here:

Are you looking to enhance your expertise in neuromuscular science? AcadeMYO is back this December with a unique opportunity to dive into myology – a fascinating and ever-evolving field. 📅 When? 9th – 11th December 💻 Where? Online This year’s programme includes: - Access to 40+ pre-recorded lectures, available from late November 2024 to early January 2025 - Three live, interactive sessions featuring workshops, evaluations, and quizzes - A chance to connect with fellow professionals in the field Spaces are limited to just 100 participants, so don’t wait to register! The deadline for payment is 6th December 2024. Explore the programme and sign up here > #NeuromuscularScience #Myology #ProfessionalDevelopment #MedicalEducation #AcadeMYO2024

This week, members of the TREAT-NMD team attended the John Walton Muscular Dystrophy Research Centre’s conference in Newcastle to commemorate an important milestone. The event brought together experts, researchers, and advocates to reflect on the remarkable progress made in neuromuscular research and to consider the possibilities the next decade holds for the field. As we look to the future, it’s clear that collaboration and innovation will continue to drive advancements that make a real difference to those affected by neuromuscular conditions. Thank you to the @jwmdrc team for hosting such an inspiring event. #NeuromuscularResearch #Collaboration #Innovation