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ASGCT
@ASGCTherapy
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Advancing knowledge, awareness, and education leading to the discovery and clinical application of genetic and cellular therapies to alleviate human disease.
Joined January 2013
❓ Did you know that about 50-60% of hearing loss cases are genetic? Changes in certain genes can disrupt how the hearing system develops and functions. ✔️ #GeneTherapy offers a promising approach to target the root causes of genetic hearing loss.
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❤️ This American Heart Month, discover the future of cardiovascular care. Join us at #AnnualMeeting2025 to hear Dr. Kiran Musunuru discuss gene editing research that could revolutionize heart disease prevention. Early rates end Feb 20! Register:
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On #WorldCancerDay, learn how CAR-T cell therapy helps your immune system recognize and fight blood cancers like leukemia and lymphoma. Watch our patient-friendly video to understand this innovative treatment: #CellTherapy #PatientEducation
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🔊 TOMORROW, Feb. 4, is the last day to submit your abstracts for #ASGCT2025! Want to present your #CGT research in front of the largest gathering of professionals in this space? Send us your work through 8 p.m. ET/5 p.m. PT on Tuesday, Feb. 4!
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We caught up with our inaugural ASGCT-@aaas Congressional Policy Fellow @AdrianaBankston to see what she's been up to in Washington, D.C. for the past several months. Learn more + apply through Feb. 24 to serve in this paid role next year.
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ASGCT's 28th Annual Meeting abstract deadline has been extended. Submit your cell and gene therapy research for #ASGCT2025 by Feb 4, 8 p.m. ET/5 p.m. PT. Learn more about abstract submission guidelines and submit your work at
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RT @CellPressNews: We are delighted to introduce Joseph C. Glorioso III, PhD, as Editor-in-Chief of Molecular Therapy (@moltherapy)—the fla…
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🗓️ Register for FREE for this event from ASGCT's Ethics Committee on Feb. 18! Join us next month for this virtual event moderated by Jodi Wolff, PhD and featuring speakers Ryan Fischer (@cureangelman) and Andrew McFadyen (@SickKidsNews).
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📣 Live Now! Join #ASGCT and #FDA today from 9 a.m.-1 p.m. ET for this free + open-to-the-public scientific workshop. Register at #ASGCTAdvocacy #AAV #CGT #celltherapy #genetherapy
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📅 We are officially TWO WEEKS AWAY from the #ASGCT2025 abstract submission deadline! If you're still working on your submission, check out these tips from ASGCT Member and abstract reviewer Kate Excoffon (@spirovant).
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Want to spend a year in Washington, D.C. working alongside legislators on #CGT policy? Apply for the ASGCT-@aaas Congressional Policy Fellowship through Feb. 24! Learn from our inaugural Fellow, Dr. Adriana Bankston + apply! #ASGCTadvocacy
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On the blog: ASGCT President Paula Cannon, PhD, explains the importance of last month's @FDA approval of #Ryoncil to treat children suffering from SR-aGVHD. Read her full statement on this first off-the-shelf allogeneic #celltherapy.
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We are thrilled to announce the launch of the @RareDiseases #LivingRareStudy – the first large-scale, long-term U.S. study focused on the real-life experiences of individuals with rare diseases. #RareDiseases #NORD #PatientEducation
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🩸 January is #NationalBloodDonorMonth! Many rare blood disorders are managed by receiving regular blood transfusions. We honor those who are able to donate their time and give hope to people with disorders like #SickleCell and #BetaThalassemia.
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Did you know: One benefit of submitting a #ASGCT2025 abstract is getting your work published in the annual @MolTherapy supplement! Your #CGT research could appear in the supplement of our prestigious journal if you send it to us by Jan. 31.
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This afternoon on behalf of ASGCT, President-Elect Terry Flotte, MD (@UMassChan) is attending the #WhiteHouseCGT forum! Organized by @WhiteHouse OSTP, speakers will cover challenges + opportunities in #CGTs, regulatory approaches, the patient perspective, + more!
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NEW @MolTherapy podcast: RNA Exon Editing with @AscidianTx' Drs. Robert Bell and Michael Ehlers. Listen + subscribe wherever you listen to podcasts!
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Today the @FDA approved #Tryngolza (also known as #Olezarsen), an investigational, first-in-class, RNA-targeted medicine for the treatment of adults with familial chylomicronemia syndrome (FCS). Read the statement from ASGCT President Paula Cannon.
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